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    Protect the Orphan Drug Tax Credit!

    This week, the House Ways and Means Committee in Congress is considering the Build Back Better Act, part of which would amend the Orphan Drug Tax Credit (ODTC) in ways that would severely undercut the original goal of the 1983 Orphan Drug Act.

    Please reach out to your members of Congress and ask them to oppose Section 138141, which alters the ODTC in the final bill

    Orhan Akman, PhD discusses antisense oligonucleotide (ASO) as a novel therapeutic approach for APBD
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    Wladimir Bocca Vieira de Rezende Pinto discusses APBD and its neuromuscular clinical presentations
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    We Are APBD
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