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    Join our APBD Tour de Friends team as we participate in the Million Dollar Bike Ride for rare disease research on June 8.

    The APBD Research Foundation’s Board of Directors will MATCH the first $40,000 raised. The dollars we raise will also be MATCHED up to $30,000 by Penn Medicine’s Orphan Disease Center (ODC). We look forward to having you join us!

    Welcome Remarks — 2022 APBD Scientific & Community Conference

    Orhan Akman, PhD discusses antisense oligonucleotide (ASO) as a novel therapeutic approach for APBD

    APBD PSA 7 13

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