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Donate today to our
end of year campaign

Moving the needle for APBD research

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    Join our VIRTUAL APBD Tour de Friends Team as we cycle for the 7th time in The Million Dollar Bike Ride for Orphan Disease Research.

    Provided our community raises $30,000 for APBD research, the Orphan Disease Center will donate a match of $30,000. Additionally, we have supporters who will match the Orphan Disease Center’s donation. That triple play promises $90,000 in research to defeat APBD!

    Welcome Remarks — 2022 APBD Scientific & Community Conference
    10:59

    Orhan Akman, PhD discusses antisense oligonucleotide (ASO) as a novel therapeutic approach for APBD
    22:43

    APBD PSA 7 13
    1:36

    We Are APBD
    6:17

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