Patient Listening Sessions with the FDA
Patient Perspectives Shared with the FDA
On December 4, 2024, the APBD Research Foundation participated in the FDA’s Listening Session on “Patient and Care Partner Perspectives on Early Enrollment into Gene Therapy Clinical Trials for Rare Diseases.”
Patient Listening Session with the FDA
On October 28, 2021, the APBD Research Foundation engaged the U.S. Food and Drug Administration (FDA) in a Patient-Led Listening Session to share the burden of APBD and the needs of our community.