September 2025 Newsletter — Foundation mourns the passing of co-founder Michael Weiss; research highlights…
Table of Contents
Honoring APBDRF co-founder Michael Weiss
ASO therapy corrects intronic variant and restores GBE activity in APBD patients’ cells
Dr. Lindsay Gill champions GSD IV research at COMBINEDBrain Summit
Henry Daumeyer joins the Foundation team as Genetic Counseling Intern
Robin Knoll hosts Pampered Chef fundraiser
Foundation launches new website
Upcoming Chat events for patients and caregivers
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