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    We invite you to join our APBD Tour de Friends Rally for Research campaign to raise $150,000 for life-saving APBD research.

    Your support funds vital APBD research, bringing us closer to treatments and improving lives.

    We’re partnering with Alex The Leukodystrophy Charity and Association for Glycogen Storage Disease-UK for a special event designed to bring our global community together to connect, share experiences, and find support.

    Welcome Remarks — 2022 APBD Scientific & Community Conference
    10:59

    Orhan Akman, PhD discusses antisense oligonucleotide (ASO) as a novel therapeutic approach for APBD
    22:43

    APBD PSA 7 13
    1:36

    We Are APBD
    6:17

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