April 2026 • 34,000+ reasons to make treatments a reality
Table of Contents
34,000 -- new research puts a number on the global burden of APBD and other forms of GSD IV
Together, we can make a difference with the 2026 Rally for Research Campaign
Only a few days left to participate in our Drug Repurposing Study!
APBDRF submits commentary to the FDA on “Individualized Therapy Pathway" guidance
APBD research spotlighted at major neurology conference
Upcoming Patient Chat and Family/Caregiver Chat