April 2026 • 34,000+ reasons to make treatments a reality

Table of Contents

  • 34,000 -- new research puts a number on the global burden of APBD and other forms of GSD IV

  • Together, we can make a difference with the 2026 Rally for Research Campaign

  • Only a few days left to participate in our Drug Repurposing Study!

  • APBDRF submits commentary to the FDA on “Individualized Therapy Pathway" guidance

  • APBD research spotlighted at major neurology conference

  • Upcoming Patient Chat and Family/Caregiver Chat

 
 

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March 2026 • Join new APBD biomarker study + major research updates