We also have important metrics that we are using to track our progress, which we will share in future communications. Please contact us at email@example.com if you have any questions and would like to learn more about our Plan.
The Plan lays out a bold, but achievable, vision for the future. It builds upon years of work and our recent successes such as the Listening Session with the FDA, the APBD Scientific Conference, the Biomarker Workshops, the APBD and GSD IV Clinical Practice Guidelines, and the study of the global prevalence of APBD and GBE1 disorders. None of them would be possible without you.
With the Plan in place to guide us, the next level of work begins, and it will take community-wide engagement.
Thank you for steadfastly supporting our work to make treatments and a cure a reality. Together, we will ensure a brighter future for patients and families affected by APBD.
Emil Weiss, Co-Founder and Co-President
Jeff Levenson, Co-President
Natacha Pires, Executive Director