Recently, the Baylor Metabolic Institute completed a six-year controlled clinical trial of Triheptanoin, an alternative energy source for APBD patients. The Adult Polyglucosan Body Disease Research Foundation (APBDRF) anticipates that the results of this drug trial will be unblinded soon. If the results are positive, the newly improved FDA processing may speed this drugs availability. The APBDRF is concerned that some of its members may require financial assistance when a drug such as Triheptanoin is approved.
What APBD drugs may be coming soon?
April 13th, 2018|